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RARE Ultragenyx Pharmaceutical Inc
交易中 02-13 10:21:58 EST
21.30
-2.20
-9.36%
最高
23.17
最低
20.79
成交量
162.79万
今开
21.54
昨收
23.50
日振幅
10.13%
总市值
20.55亿
流通市值
19.77亿
总股本
9,648万
成交额
3,538万
换手率
1.75%
流通股本
9,279万
市净率
--
ROE
--
每股收益
0.00
52周最高
--
52周最低
--
市盈率
--
股息
--
股息收益率
--
ROA
--
分时
五日
日K
周K
月K
数据加载中...
北京优虎网络科技有限公司
资讯
新帖
简况
异动解读 | 财务展望引发增长担忧,Ultragenyx Pharmaceutical盘后大跌5.32%
异动解读 · 07:01
异动解读 | 财务展望引发增长担忧,Ultragenyx Pharmaceutical盘后大跌5.32%
Ultragenyx Pharmaceutical Inc预计2026年现有产品总收入将达7.3亿至7.6亿美元
美股速递 · 05:24
Ultragenyx Pharmaceutical Inc预计2026年现有产品总收入将达7.3亿至7.6亿美元
Ultragenyx Pharmaceutical预计2026年研发与行政开支总和将较2025年持平或微降
美股速递 · 05:23
Ultragenyx Pharmaceutical预计2026年研发与行政开支总和将较2025年持平或微降
Ultragenyx Pharmaceutical预计2027年研发支出将较2025年水平下降38%,约2.8亿美元
美股速递 · 05:23
Ultragenyx Pharmaceutical预计2027年研发支出将较2025年水平下降38%,约2.8亿美元
Ultragenyx Pharmaceutical Inc 研究成果:生物标志物显著改善并带来功能性获益
美股速递 · 02-03
Ultragenyx Pharmaceutical Inc 研究成果:生物标志物显著改善并带来功能性获益
Ultragenyx公布UX111基因疗法长期积极数据:显著持续降低脑脊液硫酸乙酰肝素水平,并在桑菲利波综合征(MPS IIIA)患儿多发育领域实现临床功能持续改善
美股速递 · 02-03
Ultragenyx公布UX111基因疗法长期积极数据:显著持续降低脑脊液硫酸乙酰肝素水平,并在桑菲利波综合征(MPS IIIA)患儿多发育领域实现临床功能持续改善
Ultragenyx重新向美国FDA提交UX111基因疗法治疗A型Sanfilippo综合征的生物制品许可申请
美股速递 · 01-30
Ultragenyx重新向美国FDA提交UX111基因疗法治疗A型Sanfilippo综合征的生物制品许可申请
两项三期临床折戟致股价腰斩,杰富瑞看好Ultragenyx (RARE.US)2026年借候选药物反弹,给予“买入”评级
智通财经 · 2025-12-31
两项三期临床折戟致股价腰斩,杰富瑞看好Ultragenyx (RARE.US)2026年借候选药物反弹,给予“买入”评级
Ultragenyx完成向美国FDA滚动提交DTX401 AAV基因疗法治疗Ia型糖原贮积症的生物制品许可申请
美股速递 · 2025-12-31
Ultragenyx完成向美国FDA滚动提交DTX401 AAV基因疗法治疗Ia型糖原贮积症的生物制品许可申请
华尔街顶级分析师最新评级:DigitalBridge遭下调评级
环球市场播报 · 2025-12-31
华尔街顶级分析师最新评级:DigitalBridge遭下调评级
Ultragenyx Pharmaceutical暴跌,遗传性骨病在研药物临床试验失败
智通财经 · 2025-12-29
Ultragenyx Pharmaceutical暴跌,遗传性骨病在研药物临床试验失败
美股异动 | 治疗遗传性骨病在研药物临床试验失败 Ultragenyx Pharmaceutical(RARE.US)盘前暴跌超42%
智通财经 · 2025-12-29
美股异动 | 治疗遗传性骨病在研药物临床试验失败 Ultragenyx Pharmaceutical(RARE.US)盘前暴跌超42%
Ultragenyx公布Setrusumab(Ux143)治疗成骨不全症的三期Orbit及Cosmic研究结果
美股速递 · 2025-12-29
Ultragenyx公布Setrusumab(Ux143)治疗成骨不全症的三期Orbit及Cosmic研究结果
“圣诞节可以收礼12天”?2026年这12只股票可作节日佳礼
老虎资讯综合 · 2025-12-25
“圣诞节可以收礼12天”?2026年这12只股票可作节日佳礼
数据:RARE 2小时小涨超 11%
链捕手 · 2025-12-06
数据:RARE 2小时小涨超 11%
数据:多个代币出现冲高回落,RARE 跌超 12%
链捕手 · 2025-11-20
数据:多个代币出现冲高回落,RARE 跌超 12%
异动解读 | Ultragenyx盘中大跌11.89%,4亿美元出售Crysvita特许权使用费引发投资者担忧
异动解读 · 2025-11-05
异动解读 | Ultragenyx盘中大跌11.89%,4亿美元出售Crysvita特许权使用费引发投资者担忧
异动解读 | Ultragenyx盘前大跌11.83%,4亿美元出售Crysvita特许权使用费引发投资者担忧
异动解读 · 2025-11-05
异动解读 | Ultragenyx盘前大跌11.83%,4亿美元出售Crysvita特许权使用费引发投资者担忧
异动解读 | Ultragenyx夜盘大跌13.68%,4亿美元出售Crysvita特许权使用费引发担忧
异动解读 · 2025-11-05
异动解读 | Ultragenyx夜盘大跌13.68%,4亿美元出售Crysvita特许权使用费引发担忧
异动解读 | Ultragenyx盘后暴跌14.36%,4亿美元出售Crysvita特许权使用费引发担忧
异动解读 · 2025-11-05
异动解读 | Ultragenyx盘后暴跌14.36%,4亿美元出售Crysvita特许权使用费引发担忧
公司概况
公司名称:
Ultragenyx Pharmaceutical Inc
所属市场:
NASDAQ
上市日期:
--
主营业务:
Ultragenyx Pharmaceutical Inc.于2010年4月22日成立,是一家处于发展阶段的生物科技企业,公司随后于2011年6月在特拉华州重新注册成立。公司专注于新型产品的鉴定、收购、开发与商业化,该产品主要用于治疗罕见和极罕见的疾病,产品最初目标是用于治疗严重的,令人衰弱的代谢基因类疾病。公司目前用于治疗遗传性包涵体肌病患者的缓释唾液酸正处于临床试验第二阶段,该疾病是一种渐进式的肌肉萎缩疾病。
发行价格:
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Pharmaceutical今日盘后股价大幅下跌5.32%,引起了市场的广泛关注。然而,在生物制药行业,研发投入通常被视为未来增长的关键驱动力,因此,持平或微降的开支展望可能引发了投资者对公司未来创新能力和增长潜力的担忧,从而导致了股价的下跌。Ultragenyx Pharmaceutical的这一财务展望,可能被部分投资者解读为公司在平衡短期财务表现与长期增长投入之间做出了偏保守的选择,进而影响了市场情绪。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-1","news_top_title":null,"news_tag":"movement","news_rank":0,"length":0,"strategy_id":0,"source":"ai_movement_cn","symbols":["RARE"],"gpt_icon":0},{"id":"1103742029","title":"Ultragenyx Pharmaceutical Inc预计2026年现有产品总收入将达7.3亿至7.6亿美元","url":"https://stock-news.laohu8.com/highlight/detail?id=1103742029","media":"美股速递","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1103742029?lang=zh_cn&edition=full","pubTime":"2026-02-13 05:24","pubTimestamp":1770931452,"startTime":"0","endTime":"0","summary":"生物制药公司Ultragenyx Pharmaceutical Inc近日发布业绩展望,预计到2026年,其现有产品线带来的总收入将达到7.3亿至7.6亿美元区间。这一预测凸显了公司核心产品的市场增长潜力。\n该营收预期反映了公司对现有疗法商业化进程的充分信心。通过持续拓展适应症范围与优化市场渗透策略,Ultragenyx正稳步推进其罕见病治疗产品的全球布局。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["RARE","BK4139"],"gpt_icon":0},{"id":"1142157088","title":"Ultragenyx Pharmaceutical预计2026年研发与行政开支总和将较2025年持平或微降","url":"https://stock-news.laohu8.com/highlight/detail?id=1142157088","media":"美股速递","labels":[],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1142157088?lang=zh_cn&edition=full","pubTime":"2026-02-13 05:23","pubTimestamp":1770931393,"startTime":"0","endTime":"0","summary":"生物制药公司Ultragenyx Pharmaceutical(纳斯达克代码:RARE)近日披露财务展望,预计2026年度研发支出与销售、一般及行政开支的总和,将较2025年水平实现持平或出现低个位数百分比的下滑。这一预算规划反映出公司通过优化运营效率,在持续投入创新药物研发的同时加强成本管控的战略方向。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"0","news_top_title":null,"news_tag":"","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["BK4139","RARE"],"gpt_icon":0},{"id":"1180365196","title":"Ultragenyx Pharmaceutical预计2027年研发支出将较2025年水平下降38%,约2.8亿美元","url":"https://stock-news.laohu8.com/highlight/detail?id=1180365196","media":"美股速递","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1180365196?lang=zh_cn&edition=full","pubTime":"2026-02-13 05:23","pubTimestamp":1770931393,"startTime":"0","endTime":"0","summary":"生物制药公司Ultragenyx Pharmaceutical Inc近日发布预测,到2027年,其研发支出预计将比2025年水平减少38%,相当于约2.8亿美元。这一调整反映了公司在完成关键临床试验后,研发管线将进入相对成熟的阶段。随着多个候选药物进入商业化准备期,公司计划将资源更多投向市场推广和产品上市工作。此次研发支出的战略性缩减,有望为公司在未来几年实现盈利增长创造有利条件。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["RARE","BK4139"],"gpt_icon":0},{"id":"1118044429","title":"Ultragenyx Pharmaceutical Inc 研究成果:生物标志物显著改善并带来功能性获益","url":"https://stock-news.laohu8.com/highlight/detail?id=1118044429","media":"美股速递","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1118044429?lang=zh_cn&edition=full","pubTime":"2026-02-03 21:05","pubTimestamp":1770123913,"startTime":"0","endTime":"0","summary":"Ultragenyx Pharmaceutical Inc 公布的最新研究结果显示,其在研疗法取得了重要进展,不仅实现了生物标志物的显著改善,还为患者带来了明确的功能性获益。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["RARE","BK4139"],"gpt_icon":0},{"id":"1111118765","title":"Ultragenyx公布UX111基因疗法长期积极数据:显著持续降低脑脊液硫酸乙酰肝素水平,并在桑菲利波综合征(MPS IIIA)患儿多发育领域实现临床功能持续改善","url":"https://stock-news.laohu8.com/highlight/detail?id=1111118765","media":"美股速递","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1111118765?lang=zh_cn&edition=full","pubTime":"2026-02-03 21:02","pubTimestamp":1770123776,"startTime":"0","endTime":"0","summary":"Ultragenyx Pharmaceutical近日公布了其基因疗法UX111的长期随访数据,结果显示该疗法对桑菲利波综合征(MPS IIIA)患儿具有持续性的治疗效果。数据显示,接受UX111治疗的患者脑脊液中硫酸乙酰肝素(CSF-HS)水平出现显著且持久的降低,同时多个发育领域的临床功能均呈现持续有意义的改善。这些长期数据进一步验证了UX111基因疗法在改变疾病进程方面的潜力,为患有这种罕见神经退行性疾病的儿童带来了新的希望。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["RARE","BK4139"],"gpt_icon":0},{"id":"1170251319","title":"Ultragenyx重新向美国FDA提交UX111基因疗法治疗A型Sanfilippo综合征的生物制品许可申请","url":"https://stock-news.laohu8.com/highlight/detail?id=1170251319","media":"美股速递","labels":["productRelease"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1170251319?lang=zh_cn&edition=full","pubTime":"2026-01-30 21:32","pubTimestamp":1769779956,"startTime":"0","endTime":"0","summary":"Ultragenyx Pharmaceutical(纳斯达克代码:RARE)已正式向美国食品药品监督管理局重新递交了UX111 AAV基因疗法的生物制品许可申请。该疗法旨在治疗A型Sanfilippo综合征(又称MPS IIIA),这是一种罕见的遗传性神经退行性疾病。\n此次重新提交基于最新临床数据对申请材料进行了全面优化,标志着该基因疗法在监管审批进程中迈出关键一步。若获批,UX111将成为全球首个针对该致命性儿童罕见病的基因治疗方案。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"productRelease","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["BK4139","RARE"],"gpt_icon":0},{"id":"2595749031","title":"两项三期临床折戟致股价腰斩,杰富瑞看好Ultragenyx (RARE.US)2026年借候选药物反弹,给予“买入”评级","url":"https://stock-news.laohu8.com/highlight/detail?id=2595749031","media":"智通财经","labels":["productRelease"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/2595749031?lang=zh_cn&edition=full","pubTime":"2025-12-31 09:15","pubTimestamp":1767143744,"startTime":"0","endTime":"0","summary":"智通财经APP获悉,由于针对罕见骨病资产的两项后期临床试验失败,Ultragenyx Pharmaceutical 周一收盘下跌约 42%,但投行杰富瑞发布报告称,鉴于其管线中的其他候选药物,该公司有望在 2026 年迎来反弹。杰富瑞分析师 Maury Raycroft,给予 Ultragenyx “买入”评级并表示,公司明年可能会从 apazunersen 的三期数据公布中获益,这是一种用于治疗天使综合征的反义寡诺聚糖核酸药物。他补充称,该公司维持其 2027 年盈利指引,并将在 2026 年初明确削减开支的计划。然而,花旗对 Ultragenyx 的态度则没那么乐观。","market":"hk","thumbnail":null,"type":0,"news_type":0,"thumbnails":[],"rights":null,"property":["rate"],"language":"zh","translate_title":"","themeId":null,"theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"http://www.zhitongcaijing.com/content/detail/1387461.html","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"productRelease","news_rank":0,"length":0,"strategy_id":0,"source":"stock_zhitongcaijing","symbols":["RARE"],"gpt_icon":0},{"id":"1166494163","title":"Ultragenyx完成向美国FDA滚动提交DTX401 AAV基因疗法治疗Ia型糖原贮积症的生物制品许可申请","url":"https://stock-news.laohu8.com/highlight/detail?id=1166494163","media":"美股速递","labels":["productRelease"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1166494163?lang=zh_cn&edition=full","pubTime":"2025-12-31 05:06","pubTimestamp":1767128808,"startTime":"0","endTime":"0","summary":"Ultragenyx Pharmaceutical已顺利完成向美国食品药品监督管理局滚动提交DTX401 AAV基因疗法治疗Ia型糖原贮积症的生物制品许可申请。这一里程碑标志着该创新疗法在监管审批道路上迈出关键一步,为罕见病患者带来新的治疗希望。DTX401作为针对GSDIa的基因治疗产品,采用腺相关病毒载体技术,旨在通过单次给药实现长期疗效。若最终获批,该疗法将填补GSDIa领域精准治疗的空白,重塑罕见病治疗格局。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"productRelease","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["RARE","BK4139"],"gpt_icon":0},{"id":"2595715068","title":"华尔街顶级分析师最新评级:DigitalBridge遭下调评级","url":"https://stock-news.laohu8.com/highlight/detail?id=2595715068","media":"环球市场播报","labels":[],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/2595715068?lang=zh_cn&edition=full","pubTime":"2025-12-31 00:09","pubTimestamp":1767110940,"startTime":"0","endTime":"0","summary":"华尔街最受热议、影响市场走势的分析师研报评级,现已汇总呈现。以下为 The Fly 整理的、投资者需重点关注的当日最新评级调仓信息。 阿格斯投行将必和必拓评级从‘持有’上调至‘买入’,目标价定为 68 美元。 加拿大皇家银行资本将DigitalBridge评级从‘跑赢行业’下调至‘与行业持平’,目标价从 23 美元下调至 16 美元。该行认为,公司采用成熟供应链的标准化零部件开展研发,有望大幅降低先进核反应堆开发商通常面临的监管与技术壁垒。","market":"sh","thumbnail":null,"type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"a9c5b2ea6477641c148f3bfa413b9f24","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"https://finance.sina.com.cn/stock/usstock/c/2025-12-31/doc-inheqyvi5645186.shtml","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-1","news_top_title":null,"news_tag":"","news_rank":0,"length":0,"strategy_id":0,"source":"sina","symbols":["LU2125909916.SGD","LU0300736062.USD","BK4233","BK4585","ERO","BK4505","LU2065169927.USD","LU0054578231.USD","BK4015","LU0300736492.USD","LU0963586101.USD","IE00BLDYK493.USD","LU1923622291.USD","BK4205","RARE","BK4168","LU2065171402.SGD","BK4532","BK4160","DBRG","BK4097","MREO","RBRK","VRNS","BHP","BK4588","LU2065731478.USD","BK4182","BK4613","BK4135","CVLT","LU0274383776.USD","LU2065171311.SGD","IE00B64QTZ34.USD","NKLR","LU2125909759.SGD","LU2065170008.USD","BK4139","LU2286300806.USD"],"gpt_icon":0},{"id":"1147466746","title":"Ultragenyx Pharmaceutical暴跌,遗传性骨病在研药物临床试验失败","url":"https://stock-news.laohu8.com/highlight/detail?id=1147466746","media":"智通财经","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1147466746?lang=zh_cn&edition=full","pubTime":"2025-12-29 22:49","pubTimestamp":1767019741,"startTime":"0","endTime":"0","summary":"在后期临床试验中未达到主要疗效终点。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"3582e8b9661b08b591794cc3daf7054b","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"https://www.zhitongcaijing.com/content/detail/1386812.html","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-2","news_top_title":"Ultragenyx Pharmaceutical暴跌,遗传性骨病在研药物临床试验失败","news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":"highlight_zhitongcaijin","symbols":["RARE"],"gpt_icon":0},{"id":"2595352767","title":"美股异动 | 治疗遗传性骨病在研药物临床试验失败 Ultragenyx Pharmaceutical(RARE.US)盘前暴跌超42%","url":"https://stock-news.laohu8.com/highlight/detail?id=2595352767","media":"智通财经","labels":[],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/2595352767?lang=zh_cn&edition=full","pubTime":"2025-12-29 22:23","pubTimestamp":1767018233,"startTime":"0","endTime":"0","summary":"智通财经APP获悉,周一美股盘前,Ultragenyx Pharmaceutical(RARE.US)股价暴跌,截至发稿,该股跌超42%,报19.69美元。消息面上,该公司宣布,其一款治疗特定遗传性骨病的在研药物,在后期临床试验中未达到主要疗效终点。","market":"sh","thumbnail":null,"type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"3582e8b9661b08b591794cc3daf7054b","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"http://www.zhitongcaijing.com/content/detail/1386812.html","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-2","news_top_title":null,"news_tag":"","news_rank":0,"length":0,"strategy_id":0,"source":"stock_zhitongcaijing","symbols":["BK4139","RARE"],"gpt_icon":0},{"id":"1128746412","title":"Ultragenyx公布Setrusumab(Ux143)治疗成骨不全症的三期Orbit及Cosmic研究结果","url":"https://stock-news.laohu8.com/highlight/detail?id=1128746412","media":"美股速递","labels":[],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1128746412?lang=zh_cn&edition=full","pubTime":"2025-12-29 21:32","pubTimestamp":1767015148,"startTime":"0","endTime":"0","summary":"Ultragenyx Pharmaceutical Inc宣布,其针对成骨不全症开发的药物Setrusumab(研发代号Ux143)在三期临床试验Orbit与Cosmic中取得积极结果。这两项研究旨在评估该药物对患者骨骼强度与骨折风险的改善效果,初步数据表明其在主要终点上表现出显著疗效。公司计划基于现有结果与监管机构进一步沟通,推进后续申报流程。","market":"us","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"0","news_top_title":null,"news_tag":"","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["BK4139","RARE"],"gpt_icon":0},{"id":"1163752901","title":"“圣诞节可以收礼12天”?2026年这12只股票可作节日佳礼","url":"https://stock-news.laohu8.com/highlight/detail?id=1163752901","media":"老虎资讯综合","labels":["corporation"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1163752901?lang=zh_cn&edition=full","pubTime":"2025-12-25 15:29","pubTimestamp":1766647746,"startTime":"0","endTime":"0","summary":"特斯拉被认为是“美股七巨头”中最“顽皮”的一只股票,仅有45%的分析师给予其“买入”评级,且平均目标价低于当前股价。相比之下,罗素1000指数成分股的平均“买入”评级比例目前约为58%。大型成长股大幅上涨,就像拆开一份期盼已久的圣诞礼物。在罗素1000指数中,只有大约5%的股票,其目标价明显低于当前交易价格。即便是逆向投资者,可能也未必认为这是一份最好的“礼物”。","market":"us","thumbnail":"https://community-static.tradeup.com/news/1303599391ea8a5a388ca86bb9de75b3","type":0,"news_type":0,"thumbnails":["https://community-static.tradeup.com/news/1303599391ea8a5a388ca86bb9de75b3"],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"13d44e8d649e7e968597cd411f47871e","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":true,"source_rank":0,"column":"","sentiment":"-1","news_top_title":null,"news_tag":"corporation","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["ALK","MSFT","FRMI","Q","AUR","LOAR","QXO","VKTX","RARE","MSTR","NVDA","AMZN","TSLA"],"gpt_icon":1},{"id":"2589828371","title":"数据:RARE 2小时小涨超 11%","url":"https://stock-news.laohu8.com/highlight/detail?id=2589828371","media":"链捕手","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/2589828371?lang=zh_cn&edition=full","pubTime":"2025-12-06 17:30","pubTimestamp":1765013429,"startTime":"0","endTime":"0","summary":" ChainCatcher 消息,据币安现货数据显示,市场出现大幅波动。RARE 2小时涨幅达 11.32%。此外,ARDR 触及今日新低,跌幅为 7.15%;EGLD、LSK、PYR、CYBER、RED、RESOLV 和 WAL 均出现“冲高回落”状态,跌幅分别为 6.82%、5.29%、6.57%、5.41%、8.38% 和 6.81%。 ","market":"sh","thumbnail":null,"type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":null,"theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"https://www.chaincatcher.com/article/2226873","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"1","news_top_title":null,"news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["BK4139","RARE"],"gpt_icon":0},{"id":"2584590909","title":"数据:多个代币出现冲高回落,RARE 跌超 12%","url":"https://stock-news.laohu8.com/highlight/detail?id=2584590909","media":"链捕手","labels":["dataReport"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/2584590909?lang=zh_cn&edition=full","pubTime":"2025-11-20 11:30","pubTimestamp":1763609434,"startTime":"0","endTime":"0","summary":" ChainCatcher 消息,据币安现货数据显示,市场出现多种动态。CHR 涨幅为 6.92%,同时触及探底回升状态,ONE 涨幅为 6.49%,同样触及探底回升状态。另一方面,FET 出现“冲高回落”状态,跌幅为 5.7%。FIS、ILV 和 RARE 也分别出现“冲高回落”状态,跌幅为 10.61%、10.53% 和 12.83%。PYR 的跌幅更是达到 23.99%。 ","market":"us","thumbnail":null,"type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":null,"theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"https://www.chaincatcher.com/article/2222062","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-1","news_top_title":null,"news_tag":"dataReport","news_rank":0,"length":0,"strategy_id":0,"source":null,"symbols":["RARE","BK4139"],"gpt_icon":0},{"id":"1113313764","title":"异动解读 | Ultragenyx盘中大跌11.89%,4亿美元出售Crysvita特许权使用费引发投资者担忧","url":"https://stock-news.laohu8.com/highlight/detail?id=1113313764","media":"异动解读","labels":["movement"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1113313764?lang=zh_cn&edition=full","pubTime":"2025-11-05 22:43","pubTimestamp":1762353801,"startTime":"0","endTime":"0","summary":"罕见疾病制药公司Ultragenyx Pharmaceutical Inc今日盘中大跌11.89%,引发市场广泛关注。这一显著跌幅主要源于公司最新宣布的一项重大交易决策。据悉,Ultragenyx将其在Crysvita公司未来25%的特许权使用费权益以4亿美元的价格出售给加拿大养老基金OMERS。Crysvita是一种用于治疗罕见骨病的药物,自2018年获批以来,在相关地区的累计销售额已超过40亿美元。这笔交易引发了投资者对Ultragenyx长期收益前景的担忧。值得注意的是,Ultragenyx股价今年以来已下跌23%,此次下跌进一步加剧了投资者的忧虑。","market":"sg","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-2","news_top_title":null,"news_tag":"movement","news_rank":0,"length":0,"strategy_id":0,"source":"ai_movement_cn","symbols":["RARE"],"gpt_icon":0},{"id":"1165015812","title":"异动解读 | Ultragenyx盘前大跌11.83%,4亿美元出售Crysvita特许权使用费引发投资者担忧","url":"https://stock-news.laohu8.com/highlight/detail?id=1165015812","media":"异动解读","labels":["movement"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1165015812?lang=zh_cn&edition=full","pubTime":"2025-11-05 21:10","pubTimestamp":1762348250,"startTime":"0","endTime":"0","summary":"罕见疾病制药公司Ultragenyx Pharmaceutical Inc今日盘前大跌11.83%,引发市场广泛关注。这一跌幅主要源于公司最新宣布的一项重大交易决策。据悉,Ultragenyx将其在Crysvita公司未来25%的特许权使用费权益以4亿美元的价格出售给加拿大养老基金OMERS。Crysvita是一种用于治疗罕见骨病的药物,自2018年获批以来,在相关地区的累计销售额已超过40亿美元。这笔交易引发了投资者对Ultragenyx长期收益前景的担忧。值得注意的是,Ultragenyx股价今年以来已下跌23%,此次下跌进一步加剧了投资者的忧虑。","market":"sg","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-2","news_top_title":null,"news_tag":"movement","news_rank":0,"length":0,"strategy_id":0,"source":"ai_movement_cn","symbols":["RARE"],"gpt_icon":0},{"id":"1143181614","title":"异动解读 | Ultragenyx夜盘大跌13.68%,4亿美元出售Crysvita特许权使用费引发担忧","url":"https://stock-news.laohu8.com/highlight/detail?id=1143181614","media":"异动解读","labels":["movement"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1143181614?lang=zh_cn&edition=full","pubTime":"2025-11-05 09:19","pubTimestamp":1762305557,"startTime":"0","endTime":"0","summary":"罕见疾病制药公司Ultragenyx Pharmaceutical Inc在夜盘交易中股价大幅下跌13.68%,引发市场广泛关注。导致股价下跌的主要原因是公司宣布将其在Crysvita公司未来25%的特许权使用费权益以4亿美元的价格出售给加拿大养老基金OMERS。Crysvita是一种用于治疗罕见骨病的药物,自2018年获批以来,在相关地区的累计销售额已超过40亿美元。值得注意的是,Ultragenyx股价今年以来已下跌23%,此次下跌进一步加剧了投资者的忧虑。","market":"hk","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-2","news_top_title":null,"news_tag":"movement","news_rank":0,"length":0,"strategy_id":0,"source":"ai_movement_cn","symbols":["RARE"],"gpt_icon":0},{"id":"1192009820","title":"异动解读 | Ultragenyx盘后暴跌14.36%,4亿美元出售Crysvita特许权使用费引发担忧","url":"https://stock-news.laohu8.com/highlight/detail?id=1192009820","media":"异动解读","labels":["movement"],"top":-1,"itemType":null,"share":"https://www.laohu8.com/m/news/1192009820?lang=zh_cn&edition=full","pubTime":"2025-11-05 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Inc在盘后交易中股价大幅下跌14.36%,引发市场关注。根据公司公告,Ultragenyx将其在Crysvita公司未来25%的特许权使用费权益以4亿美元的价格出售给加拿大养老基金OMERS。根据协议,OMERS将从2028年1月开始从Crysvita在美国和加拿大的销售中获得额外的特许权使用费份额。Crysvita是一种用于治疗罕见骨病的药物,自2018年获批以来,在相关地区的累计销售额已超过40亿美元。值得注意的是,Ultragenyx股价今年以来已下跌23%,此次下跌进一步加剧了投资者的忧虑。","market":"hk","thumbnail":"","type":0,"news_type":0,"thumbnails":[],"rights":null,"property":[],"language":"zh","translate_title":"","themeId":"","theme_name":"","theme_type":"","isJumpTheme":false,"source_url":"","is_publish_highlight":false,"source_rank":0,"column":"","sentiment":"-1","news_top_title":null,"news_tag":"movement","news_rank":0,"length":0,"strategy_id":0,"source":"ai_movement_cn","symbols":["RARE"],"gpt_icon":0}],"profile":{"websiteUrl":"http://www.ultragenyx.com","stockEarnings":[{"period":"1week","weight":-0.0122},{"period":"1month","weight":-0.0253},{"period":"3month","weight":-0.2896},{"period":"6month","weight":-0.2085},{"period":"1year","weight":-0.4589},{"period":"ytd","weight":0.0217}],"compareEarnings":[{"period":"1week","weight":0.0054},{"period":"1month","weight":-0.018},{"period":"3month","weight":0.0139},{"period":"6month","weight":0.0588},{"period":"1year","weight":0.1291},{"period":"ytd","weight":-0.001}],"compareStock":{"symbol":"SPY","name":"标普500ETF"},"description":"Ultragenyx 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