赛诺菲(SNY.US)全球首创新药申报上市

智通财经05-28

智通财经APP获悉，5月28日，赛诺菲(SNY.US)宣布Venglustat的上市申请获得FDA受理并予以优先审评，用于治疗III型戈谢病(GD3)。如果获批，Venglustat将成为美国首个针对GD3相关进行性神经系统表现的治疗方案，并扩充赛诺菲为溶酶体贮积病患者提供的治疗方案。Venglustat是一种新型的口服葡萄糖神经酰胺合成酶抑制剂(GCSi)，能够强效抑制N端甲基转移酶1(...

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