uniQure(QURE.US)因基因疗法AMT-130大涨高盛唱多：峰值销售额有望达25亿美元

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智通财经APP获悉，高盛最新深度分析报告聚焦uniQure NV(QURE.US)基因疗法AMT-130在亨廷顿病治疗中的突破性进展及商业前景。据披露，该疗法已在两项剂量组临床试验中展现显著疗效——高剂量组17例患者完成36个月随访后，复合亨廷顿病评定量表显示疾病进展较自然病史减缓75%，总功能能力评分变化减缓60%，脑脊液神经丝轻链蛋白水平平均下降8.2%;低剂量组12例患者虽未直接给出对比数据...

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uniQure(QURE.US)因基因疗法AMT-130大涨 高盛唱多：峰值销售额有望达25亿美元

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uniQure(QURE.US)因基因疗法AMT-130大涨高盛唱多：峰值销售额有望达25亿美元